Biochemical genetics: News

Sanfilippo clinical trial

• A Phase III, double blinded, randomised, placebo controlled clinical trial of high dose oral Genistein Aglycone in patients with Sanfilippo Syndrome (Mucopolysaccharidosis III A, B and C) - GENiSIS2013 (PDF, 178 KB)

Genistein clinical trial

• Position Statement on the use of genistein to treat Sanfilippo disease (Mucopolysaccharidosis type IIIA-D) (PDF, 44 KB)

MPS Stem Cell Lab Newsletters

• MPS Stem Cell Lab Newsletter: Issue 1 (PDF, 196 KB)
• MPS Stem Cell Lab Newsletter: Issue 2 (PDF, 2 MB)